Ep. 218: Beyond Symptom Control: Gene Therapy for Rare Neurological Disorders

Moderator: Kleopas Kleopa (Nicosia, Cyprus)

Guest: Jo Ng (London, UK)

In this episode, Kleopas Kleopa speaks with Jo Ng about gene therapy for rare neurological disorders. They discuss the clinical potential of AAV-based therapies, key diagnostic and therapeutic considerations including early diagnosis and treatment timing, and challenges related to safety, immune responses, dosing, and long-term outcomes, with a focus on translating advances into neurological practice.